Avg. average, Vol. volume, DIPG diffuse intrinsic pontine glioma, [124I]−8H9 radioimmunotherapy omburtamab, IL13-PE38QQR interleukin-13–pseudomonas exotoxin, MTX110 aqueous panobinostat, AADC aromatic L-amino acid decarboxylase deficiency, AAV2-hAADC viral vector expressing AADC. The gene discussed is DDC; the disease is hyperinsulinemic hypoglycemia, familial, 4.