The most common grade 1/2 AEs were hyperphosphatemia (n = 9), AST elevation (n = 8), alkaline phosphatase elevation (n = 8), anemia (n = 8), fatigue (n = 6), diarrhea (n = 5), ALT elevation (n = 5), and anorexia (n = 5). The gene discussed is GPT; the disease is anemia (phenotype).