DMD and neoplasm: • AAV delivery of a miniaturized dystrophin gene improves symptoms in the Golden Retriever muscular dystrophy model without causing severe adverse events (Birch et al., 2023)• Targeted delivery of αEGFR-CRISPR-sgSOX2-LNPs resulted in a 90% inhibition of tumor growth and a 90% increase in survival for over 84 days in a xenograft HNSCC mouse model (Masarwy et al., 2025)