LAMP2 and Danon disease: Another is the Clinical Study Evaluating a Recombinant Adeno-Associated Virus Serotype 9 (rAAV9) Capsid Containing the Human Lysosome-Associated Membrane Protein 2 Isoform B (LAMP2B) Transgene (RP-A501; AAV9.LAMP2B) in Patients With Danon Disease, which will target patients with truncating LAMP2 variants (NCT06092034, ClinicalTrials.gov).