DMD and Duchenne muscular dystrophy: A number of treatments that alter dystrophin expression have been recently approved for the treatment of DMD, including exon-skipping antisense oligonucleotides (Aartsma-Rus et al., 2017), such as Exondys51 and Viltepso, and the adeno-associated viral vector-based gene therapy, ELEVIDYS (Heydemann and Siemionow, 2023).