Grade 1 or 2 hematological AEs were anemia (18.2%, 2/11) and thrombocytopenia (9.1%, 1/11) and non-hematological AEs were fatigue (27.3%, 3/11), paresthesia (18.2%, 2/11), alanine aminotransferase increase (18.2%, 2/11), aspartate aminotransferase (18.2%, 2/11), and hypokalemia (18.2%, 2/11). The gene discussed is GPT; the disease is anemia (phenotype).