DMD and Duchenne muscular dystrophy: Baseline characteristics of the patients 1–3, including the demographic data (type of DMD mutation, age at DMD diagnosis, age at enrollment, height, weight and BMI), duration on steroids before treatment and functional status (ambulatory vs. non-ambulatory), are summarized in Table 1A. The summary of DEC01 therapy dose, date of administration and completed visits and post-transplant follow-up time are provided in Table 1B.