AIPL1 and Leber congenital amaurosis 4: A similar HDR-based CRISPR/Cas9 strategy was used in order to homozygously correct the biallelic c.834G>A, p.Trp278X mutation with an efficiency of 30% in the AIPL1 gene that causes Leber Congenital Amaurosis type 4 (LCA4) [111].