Additionally, since 2014, the drug Translarna, a nonaminoglycoside drug that induces translational readthrough, has been approved by the European Medicines Agency (EMA) as an orphan drug for the treatment of Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene in ambulatory patients aged 2 years and older [46]. The gene discussed is DMD; the disease is Duchenne muscular dystrophy.