CTSG and severe combined immunodeficiency: Outline of studies about the function of miR-1246 in animal models (∆: knock-down or deletion, PDX: derived orthotopic xenograft, NOD-SCID: non-obese diabetic/severe combined immunodeficiency, NSG: NOD Cg-Prkdcscid Il2rgtm1Wjl/SzJ).