FKRP and muscular dystrophy: To date, several experimental studies in animal models have provided evidence supporting the potential therapeutic application of gene therapy (Gicquel et al., 2017; Xu et al., 2013) and cell therapy (Azzag et al., 2020; Frattini et al., 2017) for FKRP-associated muscular dystrophies, but these studies are still at early stages, and therefore, currently there are no clinical trials underway.