Ataluren (1% m/v) suspension in 0.9% saline vehicle containing 1% tween 80 as a co-solvent, and 1% carboxymethylcellulose to increase viscosity, also known as the ‘START’ formulation, was shown to rescue the corneal deficit in Pax6-deficient mice model of aniridia [10]. Here, PAX6 is linked to isolated aniridia.