Haas Haas M M Vlcek Vlcek V V Balabanov Balabanov P P European medicines agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene European medicines agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene Neuromuscul Disord Neuromuscul Disord 2015 2015 25 25 5 5 13 13 10.1016/j.nmd.2014.11.011 10.1016/j.nmd.2014.11.011 25497400 25497400. The gene discussed is DMD; the disease is Duchenne muscular dystrophy.