Grade 3 or higher AEs included neutropenia (23 patients [51%]), anemia (6 patients [13%]), alanine aminotransferase level elevation (2 patients [4%]), aspartate transaminase level elevation (1 patient [2%]), fatigue (1 patient [2%]), thrombocytopenia (1 patient [2%]), diarrhea (1 patient [2%]), and nausea (1 patient [2%]). The gene discussed is GPT; the disease is anemia (phenotype).