PSMA6 and Duchenne muscular dystrophy: The treatment of genetic diseases remains one of the central challenges in medicine, where most genetic diseases—such as Duchenne muscular dystrophy (DMD), congenital heart disease, liver alpha 1 antitrypsin deficiency, familial partial lipodystrophy, and cystic fibrosis, to name a few—can be cured only if the disease-causing mutation is corrected to the wild-type sequence.