Besides the cocktail approach, gene editing using CRISPR/Cas9 has also proven efficacious in deleting the entire DMD exons 45–55 region from the genome, accompanied by dystrophin rescue, in DMD patient-derived induced pluripotent cells (DMD iPSCs) [59] and a humanized DMD mouse model [60]. This evidence concerns the gene DMD and Duchenne muscular dystrophy.