DMD and neuromuscular disease caused by qualitative or quantitative defects of dystrophin: Current therapies are able to address several dystrophinopathy symptoms to improve the quality of life for DMD patients or delay the disease development, but they fail in halting the progression completely.7, 8, 9, 10 Gene- and cell-based approaches, on the other hand, provide promise for a cure, as they have shown abilities to correct the faulty DMD gene,11, 12 to add a modified form of the DMD gene,13, 14, 15, 16 or to generate myofibers from engrafted mesoangioblasts.17