Duchenne muscular dystrophy (DMD) is a lethal X-linked genetic disorder (affecting approximately 1 in 5000 boys) [1] caused by mutations in the ~2.4-megabase DMD gene [2] which lead to irrevocable muscle wasting owing to the absence of dystrophin in the striated muscle cell lineage [3]. The gene discussed is DMD; the disease is Duchenne muscular dystrophy.