In fact, SMN2 transgenic SMA mice with 8 (SMN2(566)+/−;mSmn−/−) or 16 copies (SMN2(566)+/+;mSmn−/−) of the transgene display no motor phenotype [34]; in other words, the SMA phenotype is rescued. The gene discussed is SMN2; the disease is proximal spinal muscular atrophy.